Generation Bio stands out for its unique approach to genetic medicine, utilizing a non-viral platform that includes a novel DNA construct, a targeted delivery system, and a proprietary manufacturing process. This platform allows for durable treatments from a single dose, the delivery of large genetic payloads, and the ability to adjust or extend expression levels in each patient. Furthermore, their scalable manufacturing process, RES, has the potential to produce hundreds of millions of doses, demonstrating their commitment to making genetic medicine accessible to a broader population worldwide.