Ultragenyx Pharmaceutical develops and commercializes therapies for rare and ultra-rare genetic diseases. It advances a diversified pipeline and brings FDA-approved drugs, like burosumab for Tumor Induced Osteomalacia and UX007 for Long-chain Fatty Acid Oxidation Disorders, to market while ensuring continuous supply for patients. The company differentiates itself through a broad portfolio focused on high-need, niche conditions and a strong emphasis on uninterrupted patient access. Its goal is to turn scientific research into accessible treatments and lead the rare-disease market.
Company Size
1,001-5,000
Company Stage
IPO
Headquarters
Novato, California
Founded
2010
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